CANbridge and UMass Chan Medical School Spinal Muscular Atrophy Gene Therapy (CAN203) Improves Lifespan and Motor Function in Mice When Administered via Intracerebroventricular Injection

BURLINGTON, Mass. & BEIJING--(BUSINESS WIRE)--Novel CANbridge/UMass spinal muscular atrophy (SMA) gene therapy improves lifespan and motor function in mice when delivered into CNS, data at ASGCT.